Ethical issues related to the access to orphan drugs in Brazil: the case of mucopolysaccharidosis type I

Background/Aims Mucopolysaccharidosis type I (MPS I) is a rare lysosomal storage disorder treated with bone marrow transplantation or enzyme replacement therapy with laronidase, a high-cost orphan drug. Laronidase was approved by the US Food and Drug Administration and the European Medicines Agency...

Full description

Saved in:  
Bibliographic Details
Authors: Boy, Raquel (Author) ; Schwartz, V. D. (Author) ; Krug, B. C. (Author) ; Santana-da-Silva, C. (Author) ; Steiner, E. (Author) ; Acosta, X. (Author) ; Ribeiro, M. (Author) ; Galera, F. (Author) ; Leivas, G. C. (Author) ; Braz, Marlene (Author)
Format: Electronic Article
Language:English
Check availability: HBZ Gateway
Journals Online & Print:
Drawer...
Fernleihe:Fernleihe für die Fachinformationsdienste
Published: BMJ Publ. 2011
In: Journal of medical ethics
Year: 2011, Volume: 37, Issue: 4, Pages: 233-239
Online Access: Presumably Free Access
Volltext (JSTOR)
Volltext (lizenzpflichtig)
Volltext (lizenzpflichtig)

Similar Items

more